The U.S. FDA approved nusinersen (now known as Spinraza) on December 23rd, 2016. The following week Biogen announced the cost of this first-ever therapy for SMA, and the SMA community went on to lose it's mind. I spend some time addressing this, plus a December update on the kiddos. Links mentioned in this episode: Kure for Kulas Ren Will Walk Arms for Asher Global Genes RAREcast - November 9, 2016 episode Follow Byrds For A Cure on: Facebook Twitter LinkedIn